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Lai Y, Liu R, Wang L, Ma XK, Li Y, Yang G, Shi L, Guo YL, Wei Z, Zhou X, Xu W, Hou Y, Miccio A, Yang B, Mou X, Yang L, Chen J. Clinical application of base editing for treating ¦Â-thalassaemia. Nature. 2026 Apr 8. doi: 10.1038/s41586-026-10342-9. Epub ahead of print. PMID: 41951736.

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